Zolgensma, onasemnogene abeparvovec
Zolgensma (onasemnogene abeparvovec) is an FDA-approved gene therapy for children under 2 with spinal muscular atrophy (SMA) caused by mutations in both SMN1 genes. Not available where you live? Your doctor may be able to request it by named-patient import. Reserve Meds coordinates the US supply and paperwork and quotes your costs in writing first.
Named-patient access overview. Zolgensma is coordinated by Reserve Meds for international patients through cross-border sourcing coordinated with your treating doctor.
Ask about Zolgensma
Tell us the medicine and your country. We reply within one business day. On WhatsApp we usually reply the same day.
About Zolgensma
Zolgensma (onasemnogene abeparvovec) is manufactured by Novartis and indicated for Spinal muscular atrophy. It is a Gene therapy (AAV) approved by the US FDA in 2019 and may be accessible to international patients through Named Patient Program or personal-import pathways.
Case active and ready to skip the regulatory walkthrough? Ask about a medicine or WhatsApp us.
How Reserve Meds coordinates Zolgensma
- Patient or treating physician submits a named-patient request.
- Clinical team verifies appropriateness of Zolgensma for the patient and destination country.
- Treating physician issues prescription and clinical justification.
- Country-specific NPP / personal-import documentation is prepared.
- Zolgensma is sourced from a US-licensed pharmaceutical wholesale partner with full serial traceability.
- Shipment is coordinated to the patient's physician or hospital pharmacy (cold-chain where required).
Clinical trials and expanded access
On 17 October 2026 we searched ClinicalTrials.gov, the clinical study registry of the US National Library of Medicine, for studies that list onasemnogene abeparvovec as an intervention. The search found studies that are recruiting or not yet recruiting. See the current list on ClinicalTrials.gov.
Whether a patient can join a trial or an expanded access program is decided by the study team or the manufacturer, together with the treating doctor. Reserve Meds does not run trials or supply investigational medicines. We can help you and your doctor read a listing and understand the route.
Access by country
Reserve Meds publishes a detailed country deep-dive for Zolgensma in every market we coordinate. Each page below covers the destination-country regulatory pathway (named-patient framework), how quotes work, indicative timelines, physician-credential requirements, and cold-chain handling for the route into that country. Tap any country to read the full deep-dive.
Start a request for Zolgensma
Send us the medicine and your country. We reply within one business day with case-specific feasibility, timeline, and a formal quote.
Frequently asked questions
How can I get Zolgensma if it is not approved or available in my country?
Reserve Meds coordinates US-sourced Zolgensma for patients through a legal named-patient pathway, working with your treating doctor. Your treating physician provides the prescription and clinical justification; Reserve Meds prepares the named-patient documentation for your country and arranges DSCSA-compliant US sourcing and delivery to your physician or hospital pharmacy.
Can I access Zolgensma through a named-patient import?
Often, yes. Named-patient access (sometimes called personal import) is the legal route we use for FDA-approved medicines such as Zolgensma. It is different from compassionate use, which covers investigational medicines through the manufacturer's own program; we do not supply investigational medicines. Eligibility and paperwork depend on the regulator in your country, and Reserve Meds maps the specific pathway for each market it coordinates.
Do I need a prescription to access Zolgensma through Reserve Meds?
Yes. Reserve Meds is not a pharmacy and does not prescribe. A valid prescription and clinical justification from your treating physician are required, and all clinical decisions remain with your physician.
How does Reserve Meds deliver Zolgensma to a patient?
Medicines are supplied through a US-licensed pharmaceutical wholesale partner, and Reserve Meds coordinates delivery of Zolgensma to your treating physician or hospital pharmacy, with appropriate handling for the product.
How long does it take, and what does Zolgensma cost through Reserve Meds?
After a short intake, the clinical team responds within one business day with case-specific feasibility, an indicative timeline, and a formal written quote. Cost depends on the destination, the prescribed regimen, and the duration of therapy, and is confirmed in writing before anything proceeds.
How do I start a request for Zolgensma?
Submit a 60-second intake through the Reserve Meds patient portal, or message our team on WhatsApp. We reply within one business day. On WhatsApp we usually reply the same day.