Conditions
156 conditions for which we help patients access specialty medicines via cross-border NPP.
Cardiology
Familial HypercholesterolemiaHeart FailureHypertrophic CardiomyopathyPulmonary Arterial HypertensionTransthyretin AmyloidosisDermatology
Alopecia AreataAtopic DermatitisHidradenitis SuppurativaPsoriasisVitiligoEndocrinology
AcromegalyCongenital Adrenal HyperplasiaCushing's SyndromeHypophosphatasiaObesityOsteoporosisType 1 DiabetesType 2 DiabetesX-linked HypophosphatemiaGastroenterology
Crohn's DiseaseEosinophilic EsophagitisEosinophilic GastroenteritisShort Bowel SyndromeUlcerative ColitisHematology
Aplastic AnemiaHemophilia AHemophilia BITPMyelodysplastic SyndromeMyelofibrosisParoxysmal Nocturnal HemoglobinuriaPolycythemia VeraSickle Cell DiseaseThalassemiavon Willebrand DiseaseHepatology
NASHPrimary Biliary CholangitisPrimary Sclerosing CholangitisImmunology
ANCA-Associated VasculitisAnkylosing SpondylitisBehçet DiseaseChronic Granulomatous DiseaseChronic Spontaneous UrticariaCommon Variable Immune DeficiencyCryopyrin-Associated Periodic SyndromeFamilial Mediterranean FeverGiant Cell ArteritisHereditary AngioedemaMuckle-Wells SyndromePsoriatic ArthritisRheumatoid ArthritisSCIDStill's DiseaseSystemic Lupus ErythematosusTakayasu ArteritisInfectious Disease
Cytomegalovirus InfectionHIVHepatitis BHepatitis CInvasive Fungal InfectionsTuberculosisMetabolic
AlkaptonuriaCystinosisFabry DiseaseGaucher DiseaseHomocystinuriaKrabbe DiseaseLysosomal Acid Lipase DeficiencyMPS I (Hurler)MPS II (Hunter)MPS III (Sanfilippo)MPS VI (Maroteaux-Lamy)Niemann-Pick DiseasePKU (Phenylketonuria)Pompe DiseaseTay-Sachs DiseaseUrea Cycle DisordersWilson DiseaseNephrology
C3 GlomerulopathyChronic Kidney DiseaseFocal Segmental GlomerulosclerosisIgA NephropathyNeurology
Alzheimer's DiseaseAmyotrophic Lateral SclerosisAngelman SyndromeAutoimmune EncephalitisBatten DiseaseCDKL5 Deficiency DisorderCIDPChronic Inflammatory Demyelinating PolyneuropathyChronic MigraineDravet SyndromeEpilepsyFragile X SyndromeFriedreich AtaxiaGuillain-Barré SyndromeHuntington's DiseaseLennox-Gastaut SyndromeMetachromatic LeukodystrophyMultiple SclerosisMyasthenia GravisNMO Spectrum DisorderNarcolepsyParkinson's DiseaseProgressive Supranuclear PalsyRestless Legs SyndromeRett SyndromeStiff Person SyndromeTuberous Sclerosis ComplexNeuromuscular
Duchenne Muscular DystrophySpinal Muscular AtrophyOncology
Acute Lymphoblastic LeukemiaAcute Myeloid LeukemiaBladder CancerBreast CancerChronic Lymphocytic LeukemiaChronic Myeloid LeukemiaColorectal CancerEndometrial CancerGastric CancerGlioblastomaHead and Neck CancerHepatocellular CarcinomaHodgkin LymphomaLung Cancer (NSCLC)MelanomaMultiple MyelomaNon-Hodgkin LymphomaOvarian CancerPancreatic CancerProstate CancerRenal Cell CarcinomaThyroid CancerOphthalmology
Diabetic RetinopathyGeographic AtrophyGlaucomaKeratoconusLeber Congenital AmaurosisNeurotrophic KeratitisRetinitis PigmentosaStargardt DiseaseUveitisWet AMDOtolaryngology
Chronic RhinosinusitisNasal PolypsPediatrics
Kawasaki DiseasePsychiatry
ADHDAutism Spectrum DisorderBipolar DisorderMajor Depressive DisorderSchizophreniaTreatment-Resistant DepressionPulmonology
COPDCystic FibrosisIdiopathic Pulmonary FibrosisSevere AsthmaSpecialty conditions (added 2026-05-16)
AchondroplasiaAcute Urticaria (Allergy)ATTR AmyloidosisAsthmaBeta-thalassemiaCDKL5 Deficiency DisorderCerebral AdrenoleukodystrophyChronic Hand EczemaCongenital Adrenal HyperplasiaCushing's DiseaseDemodex BlepharitisDesmoid TumorDiabetesDry Eye DiseaseDystrophic Epidermolysis BullosaPAH (Endothelin Receptor)Factor XIII DeficiencyFibrodysplasia Ossificans ProgressivaFriedreich's AtaxiaGlioma (CNS Tumor)Gout / HyperuricemiaGraft-versus-Host DiseaseGrowth DisordersHepatic EncephalopathyIBD (Crohn's and UC)Idiopathic Pulmonary FibrosisLeishmaniasisLeukemiaLHON (Inherited Retinal)Lupus (SLE)Lysosomal Storage DisordersMASH (NASH)Menopause Hot FlashesMigraineNasopharyngeal CancerNeuromyelitis OpticaObstructive HCMOncology Supportive CarePediatric OphthalmicPericarditisPeriodic ParalysisPneumococcal VaccinePolymyalgia RheumaticaPrimary Biliary CholangitisProgressive Familial Intrahepatic CholestasisPrurigo NodularisPyruvate Kinase DeficiencyRare Metabolic (Other)Rare OncologyRosaceaRSV PreventionSarcomaShort Bowel SyndromeSjogren's SyndromeSolid Tumor (Breast)Solid Tumor (GI)Solid Tumor (GU)Solid Tumor (GYN)Solid Tumor (Lung)Solid Tumor (Melanoma)TAFRO / ITPTransthyretin CardiomyopathyTreatment-Resistant Depressionvon Willebrand DiseaseWarm Autoimmune Hemolytic AnemiaMore condition guides
More condition pages on the site, A to Z.
- Amyotrophic Lateral Sclerosis (ALS) access in Bahrain
- Amyotrophic Lateral Sclerosis (ALS) access in Egypt
- Amyotrophic Lateral Sclerosis (ALS) access in India
- Amyotrophic Lateral Sclerosis (ALS) access in Jordan
- Amyotrophic Lateral Sclerosis (ALS) access in Kuwait
- Amyotrophic Lateral Sclerosis (ALS) access in Oman
- Amyotrophic Lateral Sclerosis (ALS) access in Pakistan
- Amyotrophic Lateral Sclerosis (ALS) access in Qatar
- Amyotrophic Lateral Sclerosis (ALS) access in Saudi Arabia
- Amyotrophic Lateral Sclerosis (ALS) access in the UAE
- Arginase 1 deficiency (hyperargininemia)
- Aromatic L-amino acid decarboxylase (AADC) deficiency
- Barth syndrome
- Batten Disease (Neuronal Ceroid Lipofuscinoses) access in Bahrain
- Batten Disease (Neuronal Ceroid Lipofuscinoses) access in Egypt
- Batten Disease (Neuronal Ceroid Lipofuscinoses) access in India
- Batten Disease (Neuronal Ceroid Lipofuscinoses) access in Jordan
- Batten Disease (Neuronal Ceroid Lipofuscinoses) access in Kuwait
- Batten Disease (Neuronal Ceroid Lipofuscinoses) access in Oman
- Batten Disease (Neuronal Ceroid Lipofuscinoses) access in Pakistan
- Batten Disease (Neuronal Ceroid Lipofuscinoses) access in Qatar
- Batten Disease (Neuronal Ceroid Lipofuscinoses) access in Saudi Arabia
- Batten Disease (Neuronal Ceroid Lipofuscinoses) access in the UAE
- Biliary tract cancer and cholangiocarcinoma
- Cystic Fibrosis access in Bahrain
- Cystic Fibrosis access in Egypt
- Cystic Fibrosis access in India
- Cystic Fibrosis access in Jordan
- Cystic Fibrosis access in Kuwait
- Cystic Fibrosis access in Oman
- Cystic Fibrosis access in Pakistan
- Cystic Fibrosis access in Qatar
- Cystic Fibrosis access in Saudi Arabia
- Cystic Fibrosis access in the UAE
- Diffuse midline glioma (H3 K27M)
- Duchenne Muscular Dystrophy (DMD) access in Bahrain
- Duchenne Muscular Dystrophy (DMD) access in Egypt
- Duchenne Muscular Dystrophy (DMD) access in India
- Duchenne Muscular Dystrophy (DMD) access in Jordan
- Duchenne Muscular Dystrophy (DMD) access in Kuwait
- Duchenne Muscular Dystrophy (DMD) access in Oman
- Duchenne Muscular Dystrophy (DMD) access in Pakistan
- Duchenne Muscular Dystrophy (DMD) access in Qatar
- Duchenne Muscular Dystrophy (DMD) access in Saudi Arabia
- Duchenne Muscular Dystrophy (DMD) access in the UAE
- Fabry Disease access in Bahrain
- Fabry Disease access in Egypt
- Fabry Disease access in India
- Fabry Disease access in Jordan
- Fabry Disease access in Kuwait
- Fabry Disease access in Oman
- Fabry Disease access in Pakistan
- Fabry Disease access in Qatar
- Fabry Disease access in Saudi Arabia
- Fabry Disease access in the UAE
- Familial chylomicronemia syndrome (FCS)
- Gaucher Disease access in Bahrain
- Gaucher Disease access in Egypt
- Gaucher Disease access in India
- Gaucher Disease access in Jordan
- Gaucher Disease access in Kuwait
- Gaucher Disease access in Oman
- Gaucher Disease access in Pakistan
- Gaucher Disease access in Qatar
- Gaucher Disease access in Saudi Arabia
- Gaucher Disease access in the UAE
- Glycogen storage disease type Ia (GSD Ia, von Gierke disease)
- Hemophilia A access in Bahrain
- Hemophilia A access in Egypt
- Hemophilia A access in India
- Hemophilia A access in Jordan
- Hemophilia A access in Kuwait
- Hemophilia A access in Oman
- Hemophilia A access in Pakistan
- Hemophilia A access in Qatar
- Hemophilia A access in Saudi Arabia
- Hemophilia A access in the UAE
- Hemophilia B access in Bahrain
- Hemophilia B access in Egypt
- Hemophilia B access in India
- Hemophilia B access in Jordan
- Hemophilia B access in Kuwait
- Hemophilia B access in Oman
- Hemophilia B access in Pakistan
- Hemophilia B access in Qatar
- Hemophilia B access in Saudi Arabia
- Hemophilia B access in the UAE
- Huntington's Disease access in Bahrain
- Huntington's Disease access in Egypt
- Huntington's Disease access in India
- Huntington's Disease access in Jordan
- Huntington's Disease access in Kuwait
- Huntington's Disease access in Oman
- Huntington's Disease access in Pakistan
- Huntington's Disease access in Qatar
- Huntington's Disease access in Saudi Arabia
- Huntington's Disease access in the UAE
- Idiopathic macular telangiectasia type 2 (MacTel)
- Leukocyte adhesion deficiency type 1 (LAD-I)
- Lung cancer
- Mantle cell lymphoma (MCL)
- Menkes disease (Menkes syndrome)
- Metachromatic Leukodystrophy (MLD) access in Bahrain
- Metachromatic Leukodystrophy (MLD) access in Egypt
- Metachromatic Leukodystrophy (MLD) access in India
- Metachromatic Leukodystrophy (MLD) access in Jordan
- Metachromatic Leukodystrophy (MLD) access in Kuwait
- Metachromatic Leukodystrophy (MLD) access in Oman
- Metachromatic Leukodystrophy (MLD) access in Pakistan
- Metachromatic Leukodystrophy (MLD) access in Qatar
- Metachromatic Leukodystrophy (MLD) access in Saudi Arabia
- Metachromatic Leukodystrophy (MLD) access in the UAE
- Mucopolysaccharidosis (MPS)
- Multiple Sclerosis (MS) access in Bahrain
- Multiple Sclerosis (MS) access in Egypt
- Multiple Sclerosis (MS) access in India
- Multiple Sclerosis (MS) access in Jordan
- Multiple Sclerosis (MS) access in Kuwait
- Multiple Sclerosis (MS) access in Oman
- Multiple Sclerosis (MS) access in Pakistan
- Multiple Sclerosis (MS) access in Qatar
- Multiple Sclerosis (MS) access in Saudi Arabia
- Multiple Sclerosis (MS) access in the UAE
- Pediatric low-grade glioma (pLGG)
- Plexiform neurofibromas in neurofibromatosis type 1 (NF1)
- Pompe Disease access in Bahrain
- Pompe Disease access in Egypt
- Pompe Disease access in India
- Pompe Disease access in Jordan
- Pompe Disease access in Kuwait
- Pompe Disease access in Oman
- Pompe Disease access in Pakistan
- Pompe Disease access in Qatar
- Pompe Disease access in Saudi Arabia
- Pompe Disease access in the UAE
- Pulmonary Arterial Hypertension (PAH) access in Bahrain
- Pulmonary Arterial Hypertension (PAH) access in Egypt
- Pulmonary Arterial Hypertension (PAH) access in India
- Pulmonary Arterial Hypertension (PAH) access in Jordan
- Pulmonary Arterial Hypertension (PAH) access in Kuwait
- Pulmonary Arterial Hypertension (PAH) access in Oman
- Pulmonary Arterial Hypertension (PAH) access in Pakistan
- Pulmonary Arterial Hypertension (PAH) access in Qatar
- Pulmonary Arterial Hypertension (PAH) access in Saudi Arabia
- Pulmonary Arterial Hypertension (PAH) access in the UAE
- Sickle Cell Disease access in Bahrain
- Sickle Cell Disease access in Egypt
- Sickle Cell Disease access in India
- Sickle Cell Disease access in Jordan
- Sickle Cell Disease access in Kuwait
- Sickle Cell Disease access in Oman
- Sickle Cell Disease access in Pakistan
- Sickle Cell Disease access in Qatar
- Sickle Cell Disease access in Saudi Arabia
- Sickle Cell Disease access in the UAE
- Small cell lung cancer (SCLC)
- Spinal Muscular Atrophy (SMA) access in Bahrain
- Spinal Muscular Atrophy (SMA) access in Egypt
- Spinal Muscular Atrophy (SMA) access in India
- Spinal Muscular Atrophy (SMA) access in Jordan
- Spinal Muscular Atrophy (SMA) access in Kuwait
- Spinal Muscular Atrophy (SMA) access in Oman
- Spinal Muscular Atrophy (SMA) access in Pakistan
- Spinal Muscular Atrophy (SMA) access in Qatar
- Spinal Muscular Atrophy (SMA) access in Saudi Arabia
- Spinal Muscular Atrophy (SMA) access in the UAE
- Synovial sarcoma
- Tenosynovial giant cell tumor (TGCT)
- Thyroid eye disease (Graves eye disease)
- von Willebrand disease global access guide
- Wiskott-Aldrich syndrome (WAS)
Priority guides
Start here: Duchenne muscular dystrophy, recently FDA-approved medicines, and key Saudi Arabia and UAE guides.